TY - JOUR
T1 - Translating SOD1 Gene Silencing toward the Clinic: A Highly Efficacious, Off-Target-free, and Biomarker-Supported Strategy for fALS
JO - Molecular Therapy : Nucleic Acids
UR - http://eprints.whiterose.ac.uk/130343/
PY - 2018/09/07
AU - Iannitti T
AU - Scarrott J
AU - Likhite S
AU - Coldicott IRP
AU - Lewis KE
AU - Heath PR
AU - Higginbottom A
AU - Myszczynska MA
AU - Milo M
AU - Hautbergue GM
AU - Meyer K et al
ED -
DO - DOI: 10.1016/j.omtn.2018.04.015
PB - Nature Publishing Group
VL - 12
SP - 75
EP - 88
Y2 - 2025/07/05
ER -