TY - JOUR T1 - Rationale, design, and methods of a randomized, controlled, open-label clinical trial with open-label extension to investigate the safety of vosoritide in infants, and young children with achondroplasia at risk of requiring cervicomedullary decompression surgery JO - Science Progress PY - 2021/03/25 AU - Savarirayan R AU - Irving M AU - Maixner W AU - Thompson D AU - Offiah AC AU - Connolly DJA AU - Raghavan A AU - Powell J AU - Kronhardt M AU - Jeha G AU - Ghani S et al ED - DO - DOI: 10.1177/00368504211003782 PB - SAGE Publications VL - 104 IS - 1 Y2 - 2025/06/25 ER -